Huntington’s disease was long thought to be caused by the slow buildup of a toxic protein, but new research has reveale | ...

The Orphan Drugs Market is experiencing significant growth due to increasing investment in rare disease research, regulatory incentives, and advancements in biotechnology. Orphan drugs are specialized ...

ClearPoint's Q4 updates: neurosurgery growth, expanding services, controlled cash burn and high-potential partner programs ...

HDBuzz reported live updates on Bluesky from the 2025 HD Therapeutics Conference. Read on for coverage of Day 1. #CHDI2025 ...

Announced alignment with the U.S. Food and Drug Administration (FDA) on key elements of the Accelerated Approval pathway for AMT-130 in ...

Announced alignment with the U.S. Food and Drug Administration (FDA) on key elements of the Accelerated Approval pathway for AMT-130 in Huntington's disease; Initiated preparations for a potential Bio ...

Rare diseases affect millions, but most remain undiagnosed and untreated. Learn about Rare Disease Day 2025, patient ...

Law enforcement officers raided the Huntington Park City Hall and the home of Mayor Karina Macias Wednesday morning. This ...

Qure's stock rises on Huntington's therapy progress and strong gene therapy pipeline. Learn about QURE stock's cost-cutting ...

Huntington’s disease is an inherited neurological disorder causing movement, cognitive, and behavioral issues. Effective ...

LETI-101 has demonstrated therapeutically relevant reductions of mutant huntingtin (HTT) protein, exceeding 80%, while preserving essential ...

Strong evidence for ALS often comes from familial forms of the disease, where specific gene mutations— for example in the ...