It acquired rights to taligurase alfa, a form of the enzyme glucocerebrosidase in development for the treatment of Gaucher's disease, from Protalix Biotherapeutics in Carmiel, Israel. Protalix has ...

My case of Gaucher disease was different from anything the ... Finally, I started a special enzyme treatment to help my symptoms. I started treatment immediately after my diagnosis.

Gaucher is a genetic disease where glucocerebroside accumulates ... NICE also said it was recommending regular NHS funding for treatments for neuroendocrine tumours (NETs) from Novartis and ...

Genzyme anticipates supply constraints of Cerezyme (imiglucerase), a treatment for Gaucher disease, and Fabrazyme (agalsidase beta), used to treat Fabry disease, while the facility shuts down for ...

In India, 32 patients, diagnosed with this condition by the Centres of Excellence (CoEs), have registered themselves with the ...

The enzyme replacement therapy (ERT) market is projected to grow significantly, rising from US$ 10,707.6 million in ...

Families of rare disease patients appeal to PM Modi and Health Minister for increased treatment funding support.

AceLink Therapeutics, Inc., a clinical-stage biotech company developing next-generation oral substrate reduction therapies (SRTs), presented interim d ...