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FDA makes history, approving Spark's eye gene therapy
Some analysts think Spark could charge as much as $1 million for a single injection of Luxturna, used to treat Leber’s congenital amaurosis, where people have a mutated RPE65 gene.
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FDA experts to vote on Spark's groundbreaking gene therapy
Advisers to the US regulator will meet today to discuss Spark Therapeutics' Luxturna ... Experts from the FDA’s Cellular, Tissue, and Gene Therapies Advisory Committee (CTGTAC) will meet ...