over placebo in children with Rett syndrome – a devastating neurological disorder caused by mutations in the MECP2 gene found on the X chromosome. The disease causes deficits in brain function ...
Rett syndrome is a devastating neurological disorder caused mainly by mutations in the MECP2 gene found on the X chromosome. The disease causes deficits in brain function that lead to behavioural ...
Indeed, REL-1017 also has significant potential in multiple additional central nervous system conditions, including movement disorders and Rett syndrome, a rare neurological disorder affecting ...
Taysha Gene Therapies' TSHA-102 tackles Rett syndrome’s root cause with its ... You see, Rett is an extremely rare disorder that’s also prevalent in women due to MECP2 gene mutations.
and rare diseases, including Rett syndrome, and other central nervous system (CNS) disorders, today announced that The Journal of Prevention of Alzheimer’s Disease (JPAD) has published peer ...