The charity run supports people affected by Neurofibromatosis, also known as NF, which is a group of incurable genetic conditions that cause tumors to grow on nerves throughout the body.

T he original poster has since deleted the tweet, and offered a half-baked apology, while also calling him out for all of the ...

Neurofibromatosis is a rare disease with the estimation of around one in 3,000 people living with this condition. However, ...

It’s important to know that an accurate diagnosis of NF1 can only be made by a physician with expertise in the diagnosis and treatment of neurofibromatosis. Because people with NF1 often have multiple ...

An international leader in advancing neurofibromatosis research, UAB serves as the national coordinating center ... These preclinical studies may serve as a foundation for future clinical trials to ...

The FDA has approved an oral, small molecule MEK inhibitor for adult and pediatric patients 2 years of age and older with ...

PITTSBURGH — Hundreds of people braved the cold weather and rain in just their underwear for a fundraiser in Pittsburgh.

The US Food and Drug Administration (FDA) has approved SpringWorks Therapeutics’ Gomekli (mirdametinib) to treat neurofibromatosis type 1 (NF1), a type of rare genetic disorder. Both adult and ...

12, 2025 – The FDA has approved a new pill for a rare genetic disorder called neurofibromatosis type ... disorder that affects about 100,000 people in the United States.

The US Food and Drug Administration (FDA) has approved SpringWorks Therapeutics’ Gomekli (mirdametinib) to treat neurofibromatosis type 1 (NF1), a rare genetic disorder affecting approximately 100,000 ...