Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...

Scholar Rock’s spinal muscular atrophy (SMA) therapy has shown benefit in muscle function in children under 12 in a pivotal ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

A higher dose of Spinraza may be more effective than the currently approved dosing schedule for maintaining motor function in ...

A pair of clinical data sets gives Novartis confidence in a new formulation of the company’s gene therapy Zolgensma for the ...

To Novartis, fresh late-stage data support the idea that its intrathecal drug, which has the same active ingredient as ...

Scientific publications and reach in the field have shown already that post-injury angiogenesis and vascular remodeling ...

A team of researchers in Japan says two of four patients who received transplantation of special stem cells showed motor ...

Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and latent forms of myostatin in order to inhibit myostatin activation.

A team of Japanese researchers reports that two out of four patients who received stem cell transplants showed improvements in motor function, marking a potential breakthrough in the treatment of ...

If there is evidence of any motor or sensory function in the area around the anus, one of four classifications is given according to the ASIA Impairment Scale. ASIA B = Sensory Incomplete. Sensory but ...