搜索优化
English
全部
Copilot
图片
视频
地图
资讯
购物
更多
航班
旅游
酒店
搜索
笔记本
Top stories
Sports
U.S.
Local
World
Science
Technology
Entertainment
Business
More
Politics
时间不限
过去 1 小时
过去 24 小时
过去 7 天
过去 30 天
按相关度排序
按时间排序
腾讯网
19 天
超70%患者获得缓解!别构小分子调节剂获FDA突破性疗法认定
这一突破性疗法认定的依据来自在携带GRIN基因功能获得性突变的小儿患者的1b期临床试验Honeycomb的积极数据。数据显示,radiprodil治疗的总体耐受性良好。符合条件的癫痫患者的中位可计数运动性癫痫发作(CMS)频率较基线减少了86%。在试验期间,71%的患者CMS减少超过50%,且7例患者中有6例在为期8周的维持期内至少80%的日子无癫痫发作。
一些您可能无法访问的结果已被隐去。
显示无法访问的结果
今日热点
Will speak on Tuesday
Israeli attack in Gaza
RU, UKR launch attacks
Iran denies US claims
Chiefs sign Tillery
SuperSonics icon dies
Staff placed on leave
Withdraws nomination
Felony gun possession arrest
Oklahoma wildfires
Severe weather outbreak
Jets sign Derrick Nnadi
Syed formally resentenced
Quake strikes Malibu area
Former NY Rep. Lowey dies
NCAA '25 brackets revealed
Survives 95 days at sea
US mulls travel ban
US expels SA ambassador
US deports Venezuelans
North Macedonia deadly fire
Electrical fire halts show
Deported despite valid visa?
Man wins $50M over burns
ISIS leader killed in Iraq
To review F-35 jets purchase
Laceration hazard recall
Man set on fire in NYC
Pleads not guilty
Cuba suffers power outage
Crew-10 arrives at ISS
Kellogg's envoy role reduced
反馈