This Founder’s Gene Therapy Company Helped Blind Kids See Again
Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.
Blind Children See After 'Remarkable' Rare Eye Disorder Breakthrough
Researchers from London's Moorfields Eye Hospital, biotech firm MeiraGTx and University College London have demonstrated that ...
Atsena Therapeutics Granted U.S. FDA Fast Track Designation for ATSN-201 Gene Therapy to ...
Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...
Atsena’s ATSN-201 gains FDA fast track status for XLRS treatment
The Phase I/II LIGHTHOUSE trial is assessing the safety and tolerability of the gene therapy in male subjects.
Daily Jang7 天
Revolutionary gene therapy gives vision to children born blind
New genetic therapy has brought “life-changing improvements” in the vision of the infants born with one of the most severe forms of childhood blindness.According to Kings College London, an ...
ExtremeTech on MSN9 天
Gene Therapy Partially Restores Sight in Legally Blind Children
A promising study out of the United Kingdom has partially restored the vision of multiple small children born legally blind.
New Atlas11 天
Gene therapy surgery restores some vision to legally blind children
Scientists in the UK have successfully used gene therapy to restore some vision to legally blind children with an inherited retinal condition. All 11 children in the clinical trial saw improvements ...
CT child born blind gets vision partially restored after 'life-changing' gene therapy in London
A Connecticut boy is among four children who were born legally blind and saw "life-changing improvements" in their vision ...
BioSpace1 天
Roche Absorbs $2.4B Impairment in Overhaul of Spark Gene Therapy Unit
In connection with Spark’s overhaul, Roche will incur approximately $2.4 billion in goodwill impairment costs. This sum takes ...
The Oxford Student6 天
CASGEVY: NHS Approves First Sickle Cell Gene Therapy
Learn how CASGEVY, the first NHS-approved CRISPR gene therapy, treats sickle cell disease through a revolutionary genetic ...