Chlorcyclizine shows promise in reducing protoporphyrin-IX accumulation and liver damage in erythropoietic protoporphyria, ...

Researchers find that allergy medicine could help patients with a rare genetic disease avoid liver transplants.

This year’s presentations included updates from the BEACON and AURORA trials of bitopertin in patients with erythropoietic protoporphyria and the Phase 1 SAD/MAD trial of DISC-3405 in healthy ...