Facioscapulohumeral muscular dystrophy (FSHD) is the third most common form of inherited muscle disease following Duchenne and myotonic dystrophy. FSHD is initially characterized by an asymmetric ...
a venture philanthropy organization dedicated to catalyzing innovation and overcoming barriers to accelerate new therapies for facioscapulohumeral muscular dystrophy (FSHD), is calling on innovators ...
Sanofi has added to its rare disease pipeline by licensing an antibody-RNA conjugate (ARC) for facioscapulohumeral muscular dystrophy (FSHD), a genetic muscle disorder, from US biotech miRecule.
The first is ARO-DUX4, which is being developed as a potential treatment for patients with facioscapulohumeral muscular dystrophy (FSHD), while ARO-DM1 is being developed to treat myotonic ...