In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Treatment with preventive heart medications can extend survival among males with Duchenne muscular dystrophy (DMD), a new ...

Duchenne muscular dystrophy (DMD) is a rare neurological ... As symptoms develop, your healthcare provider might do cardiac and pulmonary testing to evaluate heart and breathing function.

Day 90 biopsy data reported from first 3 participants dosed in Phase 1/2 INSPIRE DUCHENNE trial —— Average microdystrophin ...

Boston, USA-based biotech Solid Biosciences saw its shares rocket 36% to $5.48 yesterday, after the precision genetic ...

The Duchenne muscular dystrophy (DMD) landscape across the seven major markets (7MM) - the US, France, Germany, Italy, Spain, ...

The study, entitled “Boys With Duchenne Muscular Dystrophy Have Diastolic Dysfunction ... slices without myocardium present throughout the cardiac cycle as well as apical slices with poor ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today reported ...

Solid Biosciences has surged back into the Duchenne muscular dystrophy (DMD) gene therapy race. | Solid Biosciences has ...

Medically reviewed by Smita Patel, DO Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed ...