Less than half of patients had undergone bone monitoring, suggesting a need for better clinical guidance and management of ...

Enrollment of healthy volunteers for a Phase 1 trial testing Duchenne muscular dystrophy (DMD) treatment candidate SAT-3247 ...

Blizzard Entertainment donated 100% of the purchase price of fundraiser's online fox companion, Reven, to support DMD ...

Cumberland Pharmaceuticals Inc. (Nasdaq: CPIX), a specialty pharmaceutical company with development efforts focused on new products for rare diseases, today announced positive top-line results from ...

Utrophin increase in muscle cells after transcriptional adaptation normalises cell function in Duchenne muscular dystrophy Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is ...

An analysis revealed global trends and emerging focus areas in Duchenne muscular dystrophy (DMD) research, emphasizing the growing impact of precision medicine and gene therapies. Septal ...

While current treatments can help manage some DMD symptoms, there are no approved ... Cardiovascular Measures of All-Cause Mortality in Duchenne Muscular Dystrophy. Circ Heart Fail.

The company is evaluating whether the drug, which targets cardiac complications, might be used treat patients with other ...