The companies will work together by using the codon-optimized BBS1 AAV9 vector to minimize the vision loss caused by the ...

Viralgen and Axovia are set to form a partnership to progress the development and manufacturing of gene therapy for retinal ...

Zolgensma, an FDA-approved AAV9 therapy that targets ... “If you look at the number of vector genomes you're delivering to an individual liver hepatocyte at that dose, it's in the range of hundreds of ...

There is an urgency for improved viral vector technology to meet the needs ... RNA expression in the spinal cord of NHPs relative to AAV9, which is the naturally occurring AAV serotype that ...

The results come from five patients enrolled in the biotech's ingoing phase 1/2 study of RGX-111 – which uses an adeno-associated viral vector (AAV9) to deliver a gene coding for an enzyme that ...

The therapeutic candidate is administered through intracisternally and intravenously. The drug candidate consists of AAV9 viral vector delivering the GBA1 gene which encodes glucocerebrosidase. It is ...

New Vericheck ddPCR Empty-Full Capsid Kits for AAV Serotypes 2 and 8 Provide Precise Measurement of Viral Titer and Capsid ...

Viralgen and Axovia Therapeutics are partnering to develop and manufacture a gene therapy for the treatment of retinal ...